NCT07214727 · Phase 1 · RECRUITING

A Study to Evaluate ALN-5288 in Patients With Alzheimer's Disease

This trial is testing ALN-5288, a new drug delivered directly into the spinal fluid via injection, in people who already have Alzheimer's disease at the MCI or mild-to-moderate dementia stage. The goal right now is simply to learn whether it is safe and how the body handles it. This is a Phase 1 trial — the very first stage in human testing, focused on safety, not yet on proving the drug works.

You may qualify if

  • Is able and willing to meet all study requirements in the opinion of the Investigator
  • Has a diagnosis of Alzheimer's disease (AD) based on clinical findings supported by cerebrospinal fluid (CSF) biomarkers or positive positron emission tomography (PET) amyloid imaging within 7 years prior to screening
  • Has mild cognitive impairment (MCI) or dementia due to AD

You're excluded if

  • Has non-AD dementia
  • Has alanine aminotransferase (ALT) or aspartate aminotransferase (AST) >2× upper limit of normal (ULN)
  • Has total bilirubin >1.5×ULN
  • Has known human immunodeficiency virus infection
  • Has history of hepatitis C virus or current hepatitis B virus infection
  • Has systolic blood pressure >160 mmHg and/or a diastolic blood pressure >100 mmHg after 10 minutes of rest at screening
  • Has an estimated glomerular filtration (eGFR) of \<45 mL/min/1.73 m\^2 at screening
  • Has clinically significant ECG abnormalities at screening
  • Has uncontrolled psychiatric disease, including patients deemed by the Investigator to be at significant risk of suicide, major depressive episode, psychosis, confusional state, or violent behavior
  • Has history of bleeding diathesis or coagulopathy due to chronic conditions
  • Has a medical history of brain or spinal disease that would interfere with the IT injection and LP procedures
  • Has history of uncontrolled seizures within the last 6 months prior to Screening

The sponsor's own eligibility wording, lightly reformatted. The study team makes the final eligibility decision — worth discussing with your doctor.

Eligibility criteria as of 2026-05-14

View full record on ClinicalTrials.gov

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